Voretigene neparvovec
Cystaran is a topical ophthalmic solution containing cysteamine, designed to reduce corneal cystine crystal accumulation in patients with cystinosis. This rare genetic disorder causes cystine to build up in various organs, including the eyes, leading to potential vision problems. Cystaran is typically used as part of a comprehensive treatment regimen for managing ocular manifestations of cystinosis.
Cystaran is an eye drop medication used to treat corneal cystine crystal buildup in patients with the rare genetic disorder cystinosis.
Key facts at a glance
- RxNorm
- 1313781
- Generic
- Cystaran
- Class
- brand-name
- Brands
- —
- Availability
- rx
- Lactation
- unknown
- Routes
- —
- Forms
- —
- Regions
- US, EU, CN, JP
- Monitoring
- —
This page is for informational purposes only.
Do not use this information to diagnose yourself or to replace a physician's advice. Always consult a qualified healthcare provider before starting, stopping, or changing any medication. If you believe you are experiencing a medical emergency, call your local emergency number immediately.
Cystaran is indicated for the treatment of corneal cystine crystal accumulation in patients with cystinosis, a rare inherited lysosomal storage disorder that causes toxic cystine buildup in cells throughout the body, particularly affecting the eyes, kidneys, and other organs.
Cystaran contains cysteamine, which acts as a cystine-depleting agent. When applied topically to the eyes, it helps reduce cystine levels in corneal tissue by converting toxic cystine into a form that can be more easily cleared from cells, thereby reducing the formation of characteristic corneal crystals.
Cystaran is for topical ophthalmic use only. Common side effects may include eye burning, stinging, redness, or irritation upon application. Patients should remove contact lenses before administration and wait at least 15 minutes before reinserting. The medication typically requires frequent dosing (often every waking hour) and should be used consistently as directed by a healthcare provider. Regular ophthalmologic monitoring is recommended during treatment.
Official drug label
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This information is for educational purposes only and is not a substitute for professional medical advice, diagnosis, or treatment.
This content is for general informational and educational purposes only and is not a substitute for professional medical advice, diagnosis, or treatment. Always seek the guidance of a qualified healthcare provider with any questions you have about a medical condition, and never disregard professional medical advice or delay seeking it because of something you read here.
If you think you may have a medical emergency, call your local emergency number or go to the nearest emergency department immediately.
Medically reviewed by WellAlly Editorial Team Last reviewed July 26, 2026. · Read our editorial policy